Veronika suffered from a very rare blood disorder since early childhood. Like many other children, she benefited from Care-for-Rare science: Thanks to an international team of researchers in the United States, France, Austria, Germany, the United Kingdom, Iran, and Israel, the cause of her disease was identified. Shuttling proteins in cells requires a highly coordinated machinery — Veronika lacked a “cargo-protein” in her immune cells. As a consequence, what occurs in an orderly way in healthy cells was disordered in Veronika’s cells.
The new knowledge helped to cure her and she decided to become a physician and researcher herself! While Veronika does not need any special awareness training, many other clinicians and scientists benefit from Care-for-Rare training fellowships. Dedicated to educating and inspiring the most promising doctors and scientists, Care-for-Rare has implemented short-term and long-term training opportunities at many of the finest medical institutions in the United States.